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RARE News

New report: If Only You Knew

By admin
10 April 2024

RARE News

Nxera Pharma joins the World Orphan Drug Alliance

By admin
9 April 2024

RARE News

Eurordis to host 12th European Conference on Rare Diseases and Orphan Products (ECRD 2024)

By admin
4 April 2024

RARE News

Miami community comes together for CureDuchenne, raising nearly $2.5M since 2021

By admin
3 April 2024

RARE News

SMA Europe launches its 12th call for research

By admin
3 April 2024

RARE News

Sickle Cell Disease Association of America promotes Kevin Amado Jr.

By admin
27 March 2024

Letters

How can we get the patient heard by the regulators?

By admin
27 March 2024

RARE REV-inar

Eight challenges in developing rare disease therapies

By admin
25 March 2024

RARE News

Rare Disease Day 2024 – Call for greater awareness of X-linked adrenoleukodystrophy and cerebral adrenoleukodystrophy

By admin
20 March 2024

RARE News

Rare disease advocates learn to accelerate therapeutic development at 9th RARE Drug Development Symposium

By admin
19 March 2024

RARE News

Alnylam launches Hereditary ATTR (hATTR) Amyloidosis campaign to help shorten diagnosis time

By admin
19 March 2024

RARE News

New primer highlights latest understanding of rare inherited disease alkaptonuria

By admin
19 March 2024

RARE News

DEBRA UK asks the British public to BE the difference for EB in 2024

By admin
19 March 2024

Industry Insights

Living well today: How do we make it happen for the rare diseases community?

By admin
13 March 2024

RARE News

Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day

By admin
1 March 2024

RARE News

Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS

By admin
29 February 2024

RARE News

SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”

By admin
29 February 2024
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