RARE News

Rare disease advocates learn to accelerate therapeutic development at 9th RARE Drug Development Symposium

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19 March 2024

RARE News

Alnylam launches Hereditary ATTR (hATTR) Amyloidosis campaign to help shorten diagnosis time

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19 March 2024

RARE News

New primer highlights latest understanding of rare inherited disease alkaptonuria

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19 March 2024

RARE News

DEBRA UK asks the British public to BE the difference for EB in 2024

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19 March 2024

RARE News

Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day

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1 March 2024

RARE News

Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS

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29 February 2024

RARE News

SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”

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29 February 2024

RARE News

£1.5 million new fund launched to ‘Help the Heart’

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27 February 2024

RARE News

CureDuchenne hosts “Champions in Miami” event on March 9 to help find a cure for Duchenne muscular dystrophy

By admin

23 February 2024

RARE News

CMT Research Foundation partners to advance study of CMT type 1J by Dr Stephan Zuchner

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21 February 2024

RARE News

Patients as Partners in Clinical Research Conference 2024

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19 February 2024

RARE News

MEF2C Foundation & MUSC launch program to develop MEF2C therapeutics

By admin

9 February 2024

RARE News

National Tay-Sachs & Allied Diseases Association hosts first of its kind drug development meeting for GM2

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2 February 2024

RARE News

Get Ready to #ShowYourStripes for Rare Disease Day 2024 29th February: the rarest day of the year!

By admin

1 February 2024

RARE News

CureDuchenne announces educational events for families and caregivers of individuals with Duchenne or Becker muscular dystrophy

By admin

31 January 2024

RARE News

Sickle Cell Disease Association of America Inc. appoints two to board

By admin

29 January 2024

RARE News

American Kidney Fund announces April 30 as the first annual APOL1-mediated kidney disease (AMKD) awareness day

By admin

26 January 2024