RARE News

Sickle Cell Disease Association of America promotes Kevin Amado Jr.

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27 March 2024

RARE News

Rare Disease Day 2024 – Call for greater awareness of X-linked adrenoleukodystrophy and cerebral adrenoleukodystrophy

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20 March 2024

RARE News

Rare disease advocates learn to accelerate therapeutic development at 9th RARE Drug Development Symposium

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19 March 2024

RARE News

Alnylam launches Hereditary ATTR (hATTR) Amyloidosis campaign to help shorten diagnosis time

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19 March 2024

RARE News

New primer highlights latest understanding of rare inherited disease alkaptonuria

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19 March 2024

RARE News

DEBRA UK asks the British public to BE the difference for EB in 2024

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19 March 2024

RARE News

Launching CamRARE’s ‘The Need for a RARE Patient Passport’ Report for Rare Disease Day

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1 March 2024

RARE News

Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS

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29 February 2024

RARE News

SMA Europe launches “Care for adults living with SMA in Europe: a benchmarking report.”

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29 February 2024

RARE News

£1.5 million new fund launched to ‘Help the Heart’

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27 February 2024

RARE News

CureDuchenne hosts “Champions in Miami” event on March 9 to help find a cure for Duchenne muscular dystrophy

By admin

23 February 2024

RARE News

CMT Research Foundation partners to advance study of CMT type 1J by Dr Stephan Zuchner

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21 February 2024

RARE News

Patients as Partners in Clinical Research Conference 2024

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19 February 2024

RARE News

MEF2C Foundation & MUSC launch program to develop MEF2C therapeutics

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9 February 2024

RARE News

National Tay-Sachs & Allied Diseases Association hosts first of its kind drug development meeting for GM2

By admin

2 February 2024

RARE News

Get Ready to #ShowYourStripes for Rare Disease Day 2024 29th February: the rarest day of the year!

By admin

1 February 2024

RARE News

CureDuchenne announces educational events for families and caregivers of individuals with Duchenne or Becker muscular dystrophy

By admin

31 January 2024